Customized iPS Cell Therapy for Recessive Monogenic Retinal Degenerative Disease

Funding Activity

Website
http://purl.org/au-research/grants/nhmrc/546489

Funding Status
Closed

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Funded Activity Summary

The focus of this study is to develop a personalised treatment for certain types of retinal degenerative disease (RDD). Stem cells will be generated from the skin cells obtained from an individual with RDD. Gene therapy will then be applied to correct the underlying disease-causing mutation in the patient cells. The repaired cells will be used to generate retinal cells, which will subsequently be tested in naturally occurring RDD rodent models to determine if they have any beneficial effects.

Funded Activity Details

Start Date: 01-01-2009

End Date: 01-01-2016

Funding Scheme: Early Career Fellowships

Funding Amount: $350,714.00

Funder: National Health and Medical Research Council

Research Topics

ANZSRC Field of Research (FoR)

Gene Therapy

ANZSRC Socio-Economic Objective (SEO)

There are no SEO codes available for this funding activity

Other Keywords

Cell differentiation | Gene targeting | Gene therapy | Stem cells | Transplantation

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