Correction of Friedreich ataxia induced pluripotent stem cells by non-viral gene therapy

Funding Activity

Website
http://purl.org/au-research/grants/nhmrc/1055785

Funding Status
Closed

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Funded Activity Summary

Friedreich ataxia (FRDA) is an inherited progressive disorder of the nervous system and heart. Stem cell therapy has the potential to repair or replace damaged tissues and restore organ function in FRDA patients. The defect inherent in stem cells obtained from FRDA patients will be corrected by a gene therapy approach that will restore normal FRDA gene expression and addresses major safety concerns for the clinical use of corrected stem cells in transplantation medicine.

Funded Activity Details

Start Date: 01-01-2014

End Date: 01-01-2016

Funding Scheme: Postgraduate Scholarships

Funding Amount: $63,270.00

Funder: National Health and Medical Research Council

Research Topics

ANZSRC Field of Research (FoR)

Gene and Molecular Therapy

ANZSRC Socio-Economic Objective (SEO)

There are no SEO codes available for this funding activity

Other Keywords

Friedreich ataxia | cell biology | gene therapy | genetics | stem cells

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